Agios Pharmaceuticals, Inc.

Agios Pharmaceuticals is a biotech company that develops medicines for rare blood disorders. Its main product is PYRUKYND, a drug that treats a condition called PK deficiency, which causes red blood cells to break down too quickly. The company is also developing medicines for sickle cell disease, thalassemia (a disorder affecting how the body makes hemoglobin), and other rare blood conditions. Most of their products are still in clinical trials, meaning they are being tested for safety and effectiveness before the FDA can approve them for widespread use.